{"id":19007,"date":"2023-11-16T17:30:57","date_gmt":"2023-11-16T17:30:57","guid":{"rendered":"https:\/\/kibrisdakik.com\/index.php\/2023\/11\/16\/ingiltere-2-farkli-kan-hastaliginin-tedavisi-icin-gen-terapisinden-faydalanilan-ilaca-onay-verdi\/"},"modified":"2023-11-16T17:30:57","modified_gmt":"2023-11-16T17:30:57","slug":"ingiltere-2-farkli-kan-hastaliginin-tedavisi-icin-gen-terapisinden-faydalanilan-ilaca-onay-verdi","status":"publish","type":"post","link":"https:\/\/kibrisdakik.com\/?p=19007","title":{"rendered":"\u0130ngiltere, 2 farkl\u0131 kan hastal\u0131\u011f\u0131n\u0131n tedavisi i\u00e7in gen terapisinden faydalan\u0131lan ilaca onay verdi"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.kibristurk.com\/images\/haberler\/2023\/11\/ingiltere-2-farkli-kan-hastaliginin-tedavisi-icin-gen-terapisinden-faydalanilan-ilaca-onay-verdi-1700154564.webp\" \/><\/p>\n<p>\u0130ngiltere \u0130la\u00e7 ve Sa\u011fl\u0131k \u00dcr\u00fcnleri D\u00fczenleme Kurumundan (MHRA), yap\u0131lan a\u00e7\u0131klamada, gen d\u00fczenleme teknolojisi CRISPR&#8217;den faydalan\u0131lan &#8220;Casgevy&#8221; adl\u0131 ilac\u0131n, orak h\u00fccreli anemi ve Akdeniz anemisi (Beta Talasemi) hastal\u0131klar\u0131n\u0131n tedavisinde kullan\u0131lmas\u0131na onay verildi\u011fi ifade edildi.<\/p>\n<p>A\u00e7\u0131klamada, Casgevy&#8217;nin, 2020 Nobel Kimya \u00d6d\u00fcl\u00fc&#8217;n\u00fc kazanan 2 bilim insan\u0131 taraf\u0131ndan geli\u015ftirilen ve genleri DNA \u00fczerinde keserek d\u00fczenlemeye izin veren &#8220;gen makas\u0131&#8221; olarak da bilinen CRISPR&#8217;\u0131n kullan\u0131ld\u0131\u011f\u0131 ilk lisansl\u0131 ila\u00e7 oldu\u011fu belirtildi.<\/p>\n<p>Gen terapisi y\u00f6nteminden faydalan\u0131lan Casgevy&#8217;nin bu 2 hastal\u0131\u011f\u0131n getirdi\u011fi a\u011fr\u0131, enfeksiyon ve kans\u0131zl\u0131\u011f\u0131 ortadan kald\u0131rabilece\u011fi aktar\u0131lan a\u00e7\u0131klamada, \u015funlar kaydedildi:<\/p>\n<p>&#8220;Casgevy, hastan\u0131n kemik ili\u011fi k\u00f6k h\u00fccrelerindeki hatal\u0131 geni d\u00fczenleyerek v\u00fccudun i\u015flevsel hemoglobin \u00fcretmesini sa\u011flayacak \u015fekilde tasarlanm\u0131\u015ft\u0131r. Bunu yapmak i\u00e7in, k\u00f6k h\u00fccreler kemik ili\u011finden al\u0131n\u0131r, laboratuvar ortam\u0131nda d\u00fczenlenir ve daha sonra hastan\u0131n v\u00fccuduna tekrar a\u015f\u0131lan\u0131r.&#8221;<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u0130ngiltere \u0130la\u00e7 ve Sa\u011fl\u0131k \u00dcr\u00fcnleri D\u00fczenleme Kurumundan (MHRA), yap\u0131lan a\u00e7\u0131klamada, gen d\u00fczenleme teknolojisi CRISPR&#8217;den faydalan\u0131lan &#8220;Casgevy&#8221; adl\u0131 ilac\u0131n, orak h\u00fccreli anemi ve Akdeniz anemisi (Beta Talasemi) hastal\u0131klar\u0131n\u0131n tedavisinde kullan\u0131lmas\u0131na onay verildi\u011fi ifade edildi. A\u00e7\u0131klamada, Casgevy&#8217;nin, 2020 Nobel Kimya \u00d6d\u00fcl\u00fc&#8217;n\u00fc kazanan 2 bilim insan\u0131 taraf\u0131ndan geli\u015ftirilen ve genleri DNA \u00fczerinde keserek d\u00fczenlemeye izin veren &#8220;gen makas\u0131&#8221;<\/p>\n","protected":false},"author":1,"featured_media":19008,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[85],"tags":[],"class_list":["post-19007","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-spor"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.4 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>\u0130ngiltere, 2 farkl\u0131 kan hastal\u0131\u011f\u0131n\u0131n tedavisi i\u00e7in gen terapisinden faydalan\u0131lan ilaca onay verdi -<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/kibrisdakik.com\/?p=19007\" \/>\n<meta property=\"og:locale\" content=\"tr_TR\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"\u0130ngiltere, 2 farkl\u0131 kan hastal\u0131\u011f\u0131n\u0131n tedavisi i\u00e7in gen terapisinden faydalan\u0131lan ilaca onay verdi -\" \/>\n<meta property=\"og:description\" content=\"\u0130ngiltere \u0130la\u00e7 ve Sa\u011fl\u0131k \u00dcr\u00fcnleri D\u00fczenleme Kurumundan (MHRA), yap\u0131lan a\u00e7\u0131klamada, gen d\u00fczenleme teknolojisi CRISPR&#8217;den faydalan\u0131lan &#8220;Casgevy&#8221; adl\u0131 ilac\u0131n, orak h\u00fccreli anemi ve Akdeniz anemisi (Beta Talasemi) hastal\u0131klar\u0131n\u0131n tedavisinde kullan\u0131lmas\u0131na onay verildi\u011fi ifade edildi. 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